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Orphan status in Europe for Alexion’s Soliris in myasthenia gravis

Orphan status in Europe for Alexion’s Soliris in myasthenia gravis

01-08-2014

The European Commission has granted orphan drug designation (ODD) to US drugmaker Alexion Pharmaceuticals’…

Alexion PharmaceuticalsBiotechnologyEuropeEuropean CommissionMyasthenia gravisNeurologic disorderRare diseasesRegulationSoliris

CHMP changes mind on PTC Therapeutics’ Duchenne drug Translarna, giving a positive opinion

25-05-2014

In something of a surprise for PTC Therapeutics and observers, the European Medicines Agency’s advisory…

BiotechnologyEuropePTC TherapeuticsRare diseasesRegulationTranslarna

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