GEMMABio launches new company

8 October 2025

Philadelphia, USA-based Gemma Biotherapeutics (GEMMABio) – a global genetic medicines company - today announced the launch of Rare Therapeutics (RareTx), a clinical-stage company focused exclusively on advancing gene therapies for ultra-orphan diseases. RareTx commences operations today with a focus on several promising treatments for lysosomal storage diseases.

The start-up will leverage public-private partnerships and regional centers of excellence it has access to as an affiliate of GEMMABio, which has established key partnerships in Brazil with Fiocruz and Abu Dhabi. GEMMABio raised $34 million in seed funding last year.

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