New uniQure findings likely to diffuse hemophilia B gene therapy scare

29 March 2021

Shares of Netherlands-based gene therapy company uniQure (Nasdaq: QURE) were up more than 9% at $32.00 in pre-market US trading, as the company revealed new evidence regarding a safety scare related to its hemophilia B gene therapy.

uniQure today announced the results of a comprehensive investigation into the case of hepatocellular carcinoma (HCC) diagnosed in one patient in the HOPE-B pivotal trial of etranacogene dezaparvovec.

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