Orphan and Rare Pediatric Disease status for Theranexus' BBDF-101

12 August 2020

The US Food and Drug Administration has awarded Orphan Drug designation (ODD) and Rare Pediatric Disease designation (RPDD) to the drug candidate BBDF-101 for Batten disease, a rare, fatal, genetic disorder of the nervous system for which there is no treatment, under development by French CNS specialist Theranexus (Euronext: ALTHX).

Announced late Tuesday, the news pushed Theranexus’ shares up 6.4% to 10.80 euros in morning trading today.

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