Positive new top-line Elevidys data lifts Sarepta

26 January 2026

Shares of US rare disease specialist Sarepta Therapeutics (Nasdaq: SRPT) were up 9.5% at $23.14 late morning after it announced positive top-line three-year functional results from Part 1-treated patients in EMBARK (Study SRP-9001-301).

The global, randomized placebo-controlled Phase III study is evaluating Elevidys (delandistrogene moxeparvovec-rokl) in ambulatory individuals with Duchenne muscular dystrophy (DMD) who were aged four to seven at time of treatment and at time of last assessment were on average over nine years of age.

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