
By Dr Nicola Davies
Sickle cell disease (SCD) is a group of inherited blood disorders characterised by a single point mutation in the β-globin gene, producing abnormal haemoglobin (Hb) called HbS. This leads to red blood cells (RBCs) deforming into a sickle shape, causing chronic hemolytic anemia, vaso-occlusive crises (VOCs), organ damage and, in severe cases, premature death.1-3
This article is accessible to registered users, to continue reading please register for free. A free trial will give you access to exclusive features, interviews, round-ups and commentary from the sharpest minds in the pharmaceutical and biotechnology space for a week. If you are already a registered user please login. If your trial has come to an end, you can subscribe here.
Login to your accountTry before you buy
7 day trial access
Become a subscriber
Or £77 per month
The Pharma Letter is an extremely useful and valuable Life Sciences service that brings together a daily update on performance people and products. It’s part of the key information for keeping me informed
Chairman, Sanofi Aventis UK
Copyright © The Pharma Letter 2025 | Headless Content Management with Blaze