Gene therapy’s worth for eye disease assessed
The USA's Institute for Clinical and Economic Review (ICER) has released a Final Evidence Report assessing the comparative clinical effectiveness and value of sonpiretigene isteparvovec for the treatment of advanced retinitis pigmentosa.
Sonpiretigene isteparvovec has not yet been approved by the US Food and Drug Administration, and manufacturer Nanoscope Therape utics’ has not announced price for the USA, if the candidate is to be approved.
A majority of ICER appraisal committee panelists found that current evidence is adequate to demonstrate a net health benefit of sonpiretigene in comparison to usual care, by a vote of 10 to two.
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