MHRA approves Adzynma, first UK treatment for cTTP
The UK’s Medicines and Healthcare products Regulatory Agency (MHRA) has approved Adzynma (apadamtase alfa/cinaxadamtase alfa; rADAMTS13), the first UK treatment to treat congenital thrombotic thrombocytopenic purpura (CTTP) in patients of all ages.
The marketing authorization was granted to the UK subsidiary of Japan’s Takeda (TYO: 4502), which gained European approval for the drug in th e same indication in August last year. The drug was also approved in Japan last year and in the USA in November 2023.
CTTP is a very rare inherited blood disorder in which blood clots form in small blood vessels throughout the body. These clots can block the flow of blood and oxygen to the body’s organs, which leads to a lower-than-normal number of platelets (components that help the blood to clot) in the blood.
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