Paroxysmal Nocturnal Hemoglobinuria
Paroxysmal Nocturnal Hemoglobinuria (PNH) hit the news at the end of 2018 when the US Food and Drug Administration approved Ultomiris (ravulizumab-cwvz; Alexion) as a treatment for this very rare blood condition.1 This is ground-breaking news for a condition that is known to affect only one to nine people per million worldwide.2
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