FDA approves AstraZeneca's Wainua as a treatment for ATTRv-PN

22 December 2023

The US Food and Drug Administration has approved AstraZeneca (LSE: AZN) and Ionis Pharmaceuticals’ (Nasdaq: IONS) Wainua (eplontersen) for the treatment of the polyneuropathy of hereditary transthyretin-mediated amyloidosis in adults, commonly referred to as hATTR-PN or ATTRv-PN.

AstraZeneca noted that Wainua is the only approved medicine for the treatment of ATTRv-PN that can be self-administered via an auto-injector. The UK pharma major licensed eplontersen from Ionis in December 2021, in a deal worth a potential $3.6 billion.

According to analytics firm GlobalData, the ATTR therapy sector is forecast to reach a value of $14.1 billion across the seven major markets by 2029.

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